(Author, Department, University,
Corresponding Address and email)
Introduction Gene therapy is a genetic technology in which genes and nucleic acids (RNA or DNA) are used for the cure, treatment, or prevention of a disease. This technology can be accomplished by replacing a defective or mutated gene with a healthy copy to reduce the problem; removing or inactivating a mutated or defective gene to reduce or eliminate improper functioning, and/or introducing a new kind of gene in the body to help in the fight against disease. Initially, the technology was used for orphan diseases such as primary immunodeficiencies, but with the passage of time, ...
